Research Leaders / KOL Map

Sickle Cell Disease: Research Leaders and Landscape

The most active researchers, institutions, and subtopics in Sickle Cell Disease, from recent PubMed records. Public authorship only, every figure verifiable by PMID.

Analyzed 594 recent PubMed papers (2021-2026) matching "sickle cell disease gene therapy". Source: NLM PubMed. Generated July 2026.

Top research leaders (by recent publication volume)

#ResearcherAffiliationPapers
1Sharma AkshaySt. Jude Children's Research Hospital31
2Makani JulieMuhimbili University of Health and Allied Sciences13
3Miccio AnnaritaUniversité Paris Cité12
4Krishnamurti LakshmananYale University School of Medicine11
5Frangoul HaydarSarah Cannon Research Institute11
6Leonard AlexisSt. Jude Children's Research Hospital10
7Kanter JulieUniversity of Alabama at Birmingham9
8Locatelli FrancoIRCCS Bambino Gesù Children's Hospital8
9Chalumeau AnneUniversité Paris Cité7
10Antoniou PanagiotisAstraZeneca6
11Corbacioglu SelimUniversity of Regensburg5
12Abraham AllistairChildren's National Hospital5
13Eapen MaryMedical College of Wisconsin5
14Johnson Liza-MarieSt. Jude Children's Research Hospital5
15Malik PunamCincinnati Children's Hospital Medical Center5
16Bhatia MonicaColumbia University/New York-Presbyterian Morgan Stanley C5
17Nkya SianaMuhimbili University of Health and Allied Sciences5
18Bhoopalan Senthil VelanSt. Jude Children's Research Hospital5

Ranked by recent publication volume; names not yet disambiguated and not citation-weighted. The full brief adds ORCID disambiguation, citation weighting, and clinical-trial investigator data.

Leading institutions

St. Jude Children's Research Hospital (43), University of California (19), Boston Children's Hospital (18), Cellular and Molecular Therapeutics Branch (15), Emory University (14), Vanderbilt University Medical Center (14), Medical College of Wisconsin (12), Children's Hospital of Philadelphia (12), Children's National Hospital (11), St Jude Children's Research Hospital (10)

Active subtopics

Anemia, Sickle Cell (376), Genetic Therapy (179), Gene Editing (105), Hematopoietic Stem Cell Transplantation (88), CRISPR-Cas Systems (77), Child (73), beta-Thalassemia (57), Hydroxyurea (54)

Top journals

Blood advances (31), Blood (14), American journal of hematology (12), British journal of haematology (11), Molecular therapy : the journal of the American Society of Gene Therapy (11), Cytotherapy (10)

Representative recent papers

The future of pediatric gene therapy: CRISPR-Cas9, AI, and personalized medicine. (2026) · PMID 42469418

Targeting transcription factors associated with hemoglobinopathies: Lessons from successful interventions and implications for can (2026) · PMID 42462791

CRISPR/Cas9-Based Genome Editing: Understanding Differences in DNA Repair Pathways, Profiles, and Outcomes. (2026) · PMID 42450173

Red lines and green lights: Gene therapy for inherited erythroid disorders beyond the haemoglobinopathies. (2026) · PMID 42448320

Blood Rheology After Allogeneic Hematopoietic Stem Cell Transplantation or Gene Therapy in Sickle Cell Disease. (2026) · PMID 42448317

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